Precision Medicine

Scientists link boy’s tumor to gene therapy viruses, in rare finding - statnews.com

Thu, 14 May 2026 06:37:55 GMT

Scientists link boy’s tumor to gene therapy viruses, in rare finding statnews.com

First human GLP-1 gene therapy trial gets green light - The Hill

Sat, 16 May 2026 12:41:00 GMT

First human GLP-1 gene therapy trial gets green light The Hill

Fractyl Health (GUTS) Is Up 14.0% After First GLP-1 Gene Therapy Trial Win And Profit Turnaround - Yahoo Finance

Sat, 16 May 2026 20:13:33 GMT

Fractyl Health (GUTS) Is Up 14.0% After First GLP-1 Gene Therapy Trial Win And Profit Turnaround Yahoo Finance

Regenxbio reaps pivotal win for Duchenne gene therapy - Fierce Biotech

Thu, 14 May 2026 11:25:00 GMT

Regenxbio reaps pivotal win for Duchenne gene therapy Fierce Biotech

Half of Patients With Post-BCG Bladder Cancer Achieve CR With Nonviral Gene Therapy - MedPage Today

Sat, 16 May 2026 20:30:35 GMT

Half of Patients With Post-BCG Bladder Cancer Achieve CR With Nonviral Gene Therapy MedPage Today

Around the Helix: Cell and Gene Therapy Company Updates – May 13, 2026 - CGTLive®

Wed, 13 May 2026 22:22:15 GMT

Around the Helix: Cell and Gene Therapy Company Updates – May 13, 2026 CGTLive®

MUSC lands three spots on top 10 global list of cell and gene therapy innovations - The Medical University of South Carolina

Tue, 12 May 2026 20:35:15 GMT

MUSC lands three spots on top 10 global list of cell and gene therapy innovations The Medical University of South Carolina

REGENXBIO to push for accelerated approval of DMD gene therapy - Clinical Trials Arena

Fri, 15 May 2026 16:39:09 GMT

REGENXBIO to push for accelerated approval of DMD gene therapy Clinical Trials Arena

Weekly Rundown: GLP-1 gene therapy enters first human trial - Drug Discovery News

Thu, 14 May 2026 07:00:00 GMT

Weekly Rundown: GLP-1 gene therapy enters first human trial Drug Discovery News

ASGCT 2026: Beverly Davidson Offers Vehicle and Route for Huntington’s Disease Gene Therapy - Genetic Engineering and Biotechnology News

Fri, 15 May 2026 13:18:20 GMT

ASGCT 2026: Beverly Davidson Offers Vehicle and Route for Huntington’s Disease Gene Therapy Genetic Engineering and Biotechnology News

ASGCT 2026: Directed evolution in gene therapy - BioWorld News

Fri, 15 May 2026 13:00:00 GMT

ASGCT 2026: Directed evolution in gene therapy BioWorld News

Gene Therapy RGX-202 Meets Primary End Point in Pivotal AFFINITY DUCHENNE Study, Supporting Accelerated Approval Plans | NeurologyLive - Clinical Neurology News and Neurology Expert Insights - Neurology Live

Thu, 14 May 2026 20:08:08 GMT

Gene Therapy RGX-202 Meets Primary End Point in Pivotal AFFINITY DUCHENNE Study, Supporting Accelerated Approval Plans | NeurologyLive - Clinical Neurology News and Neurology Expert Insights Neurology Live

First Clinical Trial for a GLP-1 Gene Therapy Greenlit in Europe - Inside Precision Medicine

Tue, 12 May 2026 18:31:10 GMT

First Clinical Trial for a GLP-1 Gene Therapy Greenlit in Europe Inside Precision Medicine

Grace Science's Gene Therapy Improves Motor Skills in Patients With NGLY1 Deficiency in Trial - Precision Medicine Online

Fri, 15 May 2026 20:44:56 GMT

Grace Science's Gene Therapy Improves Motor Skills in Patients With NGLY1 Deficiency in Trial Precision Medicine Online

MHRA launches UK-wide gene therapy consultation - EMJ

Fri, 15 May 2026 15:06:10 GMT

MHRA launches UK-wide gene therapy consultation EMJ

Experts discus new gene therapy helping children with rare genetic disorder - WPLG Local 10

Thu, 14 May 2026 22:03:27 GMT

Experts discus new gene therapy helping children with rare genetic disorder WPLG Local 10

29th Annual Meeting of the American Society for Gene and Cell Therapy - BioSpace

Tue, 12 May 2026 20:35:37 GMT

29th Annual Meeting of the American Society for Gene and Cell Therapy BioSpace

Regenxbio says Duchenne gene therapy succeeded in clinical trial, paving way for FDA submission - statnews.com

Thu, 14 May 2026 11:00:36 GMT

Regenxbio says Duchenne gene therapy succeeded in clinical trial, paving way for FDA submission statnews.com

ASGCT 2026: GS-100 Gene Therapy Demonstrates Early Activity in NGLY1 Deficiency - CGTLive®

Thu, 14 May 2026 15:27:19 GMT

ASGCT 2026: GS-100 Gene Therapy Demonstrates Early Activity in NGLY1 Deficiency CGTLive®

ASGCT Q1 Landscape Report Paints Positive Picture for Gene and RNA Therapy - Genetic Engineering and Biotechnology News

Fri, 15 May 2026 16:59:29 GMT

ASGCT Q1 Landscape Report Paints Positive Picture for Gene and RNA Therapy Genetic Engineering and Biotechnology News

Regenxbio eyes 2027 launch for DMD gene therapy, but investors wary - FirstWord Pharma

Thu, 14 May 2026 20:16:15 GMT

Regenxbio eyes 2027 launch for DMD gene therapy, but investors wary FirstWord Pharma

Hearing Loss Gene Therapy Improves Language Development, Data at ASGCT Show - Precision Medicine Online

Thu, 14 May 2026 12:16:28 GMT

Hearing Loss Gene Therapy Improves Language Development, Data at ASGCT Show Precision Medicine Online

With new data, Regenxbio to seek FDA approval of Duchenne gene therapy - BioPharma Dive

Thu, 14 May 2026 13:59:37 GMT

With new data, Regenxbio to seek FDA approval of Duchenne gene therapy BioPharma Dive

Latham & Watkins Advises LEO Pharma in Acquisition of Replay Gene Therapy Platform - Latham & Watkins LLP

Thu, 14 May 2026 17:31:40 GMT

Latham & Watkins Advises LEO Pharma in Acquisition of Replay Gene Therapy Platform Latham & Watkins LLP

Abeona downgrades eye disease gene therapies in favour of cancer cell therapy - FirstWord Pharma

Wed, 13 May 2026 19:15:52 GMT

Abeona downgrades eye disease gene therapies in favour of cancer cell therapy FirstWord Pharma

Regenxbio's Duchenne gene therapy clears phase 3 hurdle - pharmaphorum

Thu, 14 May 2026 12:19:00 GMT

Regenxbio's Duchenne gene therapy clears phase 3 hurdle pharmaphorum

AAV9 Gene Therapy in Type II GM1 Gangliosidosis — A Phase 1–2 Trial - The New England Journal of Medicine

Fri, 06 Feb 2026 08:00:00 GMT

AAV9 Gene Therapy in Type II GM1 Gangliosidosis — A Phase 1–2 Trial The New England Journal of Medicine

HealthCast: New gene therapy helping children with rare genetic disorder - WPLG Local 10

Thu, 14 May 2026 22:07:26 GMT

HealthCast: New gene therapy helping children with rare genetic disorder WPLG Local 10

Preclinical DMD gene therapy GB703 debuts as GEMMABio advances SMA program - Contemporary Pediatrics

Thu, 14 May 2026 17:46:24 GMT

Preclinical DMD gene therapy GB703 debuts as GEMMABio advances SMA program Contemporary Pediatrics

Cleveland Clinic First-In-Human Trial of CRISPR Gene-Editing Therapy Shown to Safely Lower Cholesterol and Triglycerides - Cleveland Clinic Newsroom

Sat, 08 Nov 2025 08:00:00 GMT

Cleveland Clinic First-In-Human Trial of CRISPR Gene-Editing Therapy Shown to Safely Lower Cholesterol and Triglycerides Cleveland Clinic Newsroom

Andelyn Biosciences Receives Dark Horse Consulting Certification of Gene Therapy Manufacturing Systems and Capabilities within its Initiative for Certification of Manufacturing Capabilities (ICMC™) Program - PR Newswire

Wed, 13 May 2026 12:00:00 GMT

Andelyn Biosciences Receives Dark Horse Consulting Certification of Gene Therapy Manufacturing Systems and Capabilities within its Initiative for Certification of Manufacturing Capabilities (ICMC™) Program PR Newswire

American Society of Gene and Cell Therapy Awards Beverly L. Davidson, PhD, Outstanding Achievement Award - PR Newswire

Thu, 14 May 2026 20:13:00 GMT

American Society of Gene and Cell Therapy Awards Beverly L. Davidson, PhD, Outstanding Achievement Award PR Newswire

Encoded Therapeutics' Dravet Gene Therapy Data Suggest Sirolimus May Blunt Benefit - Precision Medicine Online

Thu, 14 May 2026 13:33:27 GMT

Encoded Therapeutics' Dravet Gene Therapy Data Suggest Sirolimus May Blunt Benefit Precision Medicine Online

ASGCT Debuts Initiative to Correct 'Market Failure' in Rare Disease Gene Therapies - Precision Medicine Online

Fri, 15 May 2026 13:51:00 GMT

ASGCT Debuts Initiative to Correct 'Market Failure' in Rare Disease Gene Therapies Precision Medicine Online

Experimental gene therapy raises hope for children with fatal neurological disease - Brunel University

Thu, 14 May 2026 07:44:32 GMT

Experimental gene therapy raises hope for children with fatal neurological disease Brunel University

Encoded's Dravet gene therapy holds up, but immune suppression may limit peak response - FirstWord Pharma

Wed, 13 May 2026 15:39:22 GMT

Encoded's Dravet gene therapy holds up, but immune suppression may limit peak response FirstWord Pharma

Gene therapy heals broken hearts: No surgery needed! - WGEM

Tue, 12 May 2026 22:49:00 GMT

Gene therapy heals broken hearts: No surgery needed! WGEM

First-in-human trial of CRISPR gene-editing therapy safely lowered cholesterol, triglycerides - www.heart.org

Sat, 08 Nov 2025 08:00:00 GMT

First-in-human trial of CRISPR gene-editing therapy safely lowered cholesterol, triglycerides www.heart.org

Therapeutic applications of CRISPR-Cas9 gene editing - Frontiers

Sat, 29 Nov 2025 15:40:54 GMT

Therapeutic applications of CRISPR-Cas9 gene editing Frontiers

World's First One-Time GLP-1 Gene Therapy Enters Human Trials - 조선일보

Thu, 14 May 2026 08:13:24 GMT

World's First One-Time GLP-1 Gene Therapy Enters Human Trials 조선일보

FDA fast-tracks first inhalable gene therapy for lung cancer - The Lancet

Thu, 19 Feb 2026 08:00:00 GMT

FDA fast-tracks first inhalable gene therapy for lung cancer The Lancet

Aradigm aims high, shoots for bringing payers, providers, patients and manufacturers together to solve cell and gene therapy access, financial risk problems - Managed Healthcare Executive

Fri, 15 May 2026 12:26:37 GMT

Aradigm aims high, shoots for bringing payers, providers, patients and manufacturers together to solve cell and gene therapy access, financial risk problems Managed Healthcare Executive

#ASGCT26: Encoded’s gene therapy reduced seizures in Dravet syndrome - Endpoints News

Thu, 14 May 2026 18:50:00 GMT

#ASGCT26: Encoded’s gene therapy reduced seizures in Dravet syndrome Endpoints News

Should First FDA-Approved Gene Therapy for Genetic Hearing Loss Require Action From Regeneron Pharmaceuticals (REGN) Investors? - simplywall.st

Fri, 15 May 2026 12:39:18 GMT

Should First FDA-Approved Gene Therapy for Genetic Hearing Loss Require Action From Regeneron Pharmaceuticals (REGN) Investors? simplywall.st

Encoded Therapeutics Advances ETX101 Toward Pivotal Stage and Expands Gene Therapy Pipeline - TipRanks

Sat, 16 May 2026 16:15:14 GMT

Encoded Therapeutics Advances ETX101 Toward Pivotal Stage and Expands Gene Therapy Pipeline TipRanks

Cirsium Biosciences Deepens Gene Therapy Footprint With Dyno Network Role and ASGCT Data Push - TipRanks

Sat, 16 May 2026 13:22:31 GMT

Cirsium Biosciences Deepens Gene Therapy Footprint With Dyno Network Role and ASGCT Data Push TipRanks

FDA approves first gene therapy for genetic hearing loss - NBC News

Thu, 23 Apr 2026 07:00:00 GMT

FDA approves first gene therapy for genetic hearing loss NBC News

Hematopoietic Stem-Cell Gene Therapy for Cystinosis - The New England Journal of Medicine

Wed, 18 Feb 2026 22:10:49 GMT

Hematopoietic Stem-Cell Gene Therapy for Cystinosis The New England Journal of Medicine

Why Cell and Gene Therapy's Biggest Barrier Isn't Scientific - AJMC

Fri, 01 May 2026 07:00:00 GMT

Why Cell and Gene Therapy's Biggest Barrier Isn't Scientific AJMC

MHRA opens UK-wide consultation on redefining gene therapies - GOV.UK

Mon, 11 May 2026 13:00:52 GMT

MHRA opens UK-wide consultation on redefining gene therapies GOV.UK

Gene Therapy to Treat Profound Hearing Loss - The New England Journal of Medicine

Mon, 13 Apr 2026 14:00:30 GMT

Gene Therapy to Treat Profound Hearing Loss The New England Journal of Medicine

Phase 1 Trial of CRISPR-Cas9 Gene Editing Targeting ANGPTL3 - The New England Journal of Medicine

Sat, 08 Nov 2025 08:00:00 GMT

Phase 1 Trial of CRISPR-Cas9 Gene Editing Targeting ANGPTL3 The New England Journal of Medicine

Dyno Therapeutics Launches Two New AAV Capsids and AI Platform for Rare Disease Therapeutic Development at the 2026 American Society of Gene & Cell Therapy (ASGCT) Annual Meeting - BioSpace

Thu, 14 May 2026 05:49:18 GMT

Dyno Therapeutics Launches Two New AAV Capsids and AI Platform for Rare Disease Therapeutic Development at the 2026 American Society of Gene & Cell Therapy (ASGCT) Annual Meeting BioSpace

CRISPR-Cas12a Gene Editing of HBG1 and HBG2 Promoters to Treat Sickle Cell Disease - The New England Journal of Medicine

Wed, 01 Apr 2026 21:10:56 GMT

CRISPR-Cas12a Gene Editing of HBG1 and HBG2 Promoters to Treat Sickle Cell Disease The New England Journal of Medicine

2 New York brothers undergo gene therapy treatment to recover hearing - WQAD

Tue, 12 May 2026 16:39:00 GMT

2 New York brothers undergo gene therapy treatment to recover hearing WQAD

Gene therapy ‘switch’ may offer non-addictive pain relief - Penn Medicine

Wed, 07 Jan 2026 08:00:00 GMT

Gene therapy ‘switch’ may offer non-addictive pain relief Penn Medicine

Could CRISPR really cure these diseases? - Labiotech.eu

Mon, 09 Mar 2026 07:00:00 GMT

Could CRISPR really cure these diseases? Labiotech.eu

Navigating Cell And Gene Therapy Risk In Medicaid: Lessons From The States - Health Affairs

Thu, 19 Feb 2026 18:05:53 GMT

Navigating Cell And Gene Therapy Risk In Medicaid: Lessons From The States Health Affairs

Gene therapy works for bubble boy disease - Science | AAAS

Fri, 17 Apr 2026 07:00:00 GMT

Gene therapy works for bubble boy disease Science | AAAS

Tenaya reports interim gene therapy trial results for heart condition - Investing.com

Fri, 15 May 2026 10:07:47 GMT

Tenaya reports interim gene therapy trial results for heart condition Investing.com

UMass Chan licenses gene therapy for maple syrup urine disease to Plowshare Therapies - UMass Chan Medical School

Mon, 27 Apr 2026 17:20:11 GMT

UMass Chan licenses gene therapy for maple syrup urine disease to Plowshare Therapies UMass Chan Medical School

Fractyl Health's Rejuva Gene Therapy Enters Clinical Trials for One-Time Treatment - 조선일보

Thu, 14 May 2026 15:38:07 GMT

Fractyl Health's Rejuva Gene Therapy Enters Clinical Trials for One-Time Treatment 조선일보

FDA Grants Accelerated Approval to Otarmeni, First and Only Gene Therapy for Genetic Hearing Loss - Pharmacy Times

Thu, 23 Apr 2026 07:00:00 GMT

FDA Grants Accelerated Approval to Otarmeni, First and Only Gene Therapy for Genetic Hearing Loss Pharmacy Times

Regenxbio's Duchenne study succeeded. Will it be enough to convince the FDA? - Endpoints News

Thu, 14 May 2026 11:00:00 GMT

Regenxbio's Duchenne study succeeded. Will it be enough to convince the FDA? Endpoints News

DB-OTO Gene Therapy for Inherited Deafness - The New England Journal of Medicine

Sun, 12 Oct 2025 07:00:00 GMT

DB-OTO Gene Therapy for Inherited Deafness The New England Journal of Medicine

Inside UCB’s new gene therapy facility - UCB

Fri, 24 Apr 2026 07:00:00 GMT

Inside UCB’s new gene therapy facility UCB

A Look At Fractyl Health (GUTS) Valuation After New Gene Therapy Trial Approval And First Quarter Net Income - Yahoo Finance

Thu, 14 May 2026 13:19:04 GMT

A Look At Fractyl Health (GUTS) Valuation After New Gene Therapy Trial Approval And First Quarter Net Income Yahoo Finance

OTP Town Hall — October 2025 Town Hall - fda.gov

Wed, 31 Dec 2025 08:00:00 GMT

OTP Town Hall — October 2025 Town Hall fda.gov

TNYA: TN-401 gene therapy achieved sustained arrhythmia reduction and strong safety in PKP2-ARVC - TradingView

Fri, 15 May 2026 16:39:44 GMT

TNYA: TN-401 gene therapy achieved sustained arrhythmia reduction and strong safety in PKP2-ARVC TradingView

TNYA: TN-401 gene therapy reduced arrhythmia burden and was well tolerated in PKP2-associated ARVC - TradingView

Fri, 15 May 2026 13:31:00 GMT

TNYA: TN-401 gene therapy reduced arrhythmia burden and was well tolerated in PKP2-associated ARVC TradingView

FDA fully releases clinical hold on Intellia CRISPR gene therapy trials - Fierce Biotech

Mon, 02 Mar 2026 08:00:00 GMT

FDA fully releases clinical hold on Intellia CRISPR gene therapy trials Fierce Biotech

Factor IX-Padua AAV gene therapy in hemophilia B: phases 1/2 and 3 trials - Nature

Thu, 20 Nov 2025 08:00:00 GMT

Factor IX-Padua AAV gene therapy in hemophilia B: phases 1/2 and 3 trials Nature

How Teamwork Built a Customized CRISPR Gene Therapy - the-scientist.com

Fri, 24 Oct 2025 07:00:00 GMT

How Teamwork Built a Customized CRISPR Gene Therapy the-scientist.com

Gene therapy for cardiac and vascular disease - Nature

Thu, 09 Apr 2026 13:27:01 GMT

Gene therapy for cardiac and vascular disease Nature

Future of Cell and Gene Therapy Market 2026 | Market is set to reach - openPR.com

Fri, 15 May 2026 09:57:41 GMT

Future of Cell and Gene Therapy Market 2026 | Market is set to reach openPR.com

Cost-Effectiveness of Gene Therapy for Sickle Cell Disease in Uganda: Tailoring High-Income Evidence to Uganda’s Context - February 26, 2026 - USC Schaeffer

Thu, 26 Feb 2026 08:00:00 GMT

Cost-Effectiveness of Gene Therapy for Sickle Cell Disease in Uganda: Tailoring High-Income Evidence to Uganda’s Context - February 26, 2026 USC Schaeffer

Doctoral student uses machine learning to transform gene therapy - The University of North Carolina at Chapel Hill

Fri, 17 Apr 2026 12:36:24 GMT

Doctoral student uses machine learning to transform gene therapy The University of North Carolina at Chapel Hill

AAV-delivered UGA suppressor tRNA for disease-agnostic in vivo gene therapy - Nature

Mon, 02 Feb 2026 08:00:00 GMT

AAV-delivered UGA suppressor tRNA for disease-agnostic in vivo gene therapy Nature

Tenaya Therapeutics' Gene Therapy Data Highlights Early Heart Rhythm Improvements - Benzinga

Fri, 15 May 2026 14:11:24 GMT

Tenaya Therapeutics' Gene Therapy Data Highlights Early Heart Rhythm Improvements Benzinga

New study shows gene therapy could be HIV cure - Dallas Voice

Tue, 12 May 2026 16:50:33 GMT

New study shows gene therapy could be HIV cure Dallas Voice

Fractyl wins greenlight to move GLP-1 gene therapy into the clinic - FirstWord Pharma

Mon, 11 May 2026 06:55:36 GMT

Fractyl wins greenlight to move GLP-1 gene therapy into the clinic FirstWord Pharma

CGT Catapult backs AI platform for gene therapy delivery - Pharmafile

Tue, 12 May 2026 09:03:00 GMT

CGT Catapult backs AI platform for gene therapy delivery Pharmafile

Cell and Gene Therapy Market Expected to Reach USD 105.83 Billion - openPR.com

Fri, 15 May 2026 11:34:49 GMT

Cell and Gene Therapy Market Expected to Reach USD 105.83 Billion openPR.com

Encoded Therapeutics Presents New Clinical Data from POLARIS Phase 1/2 Trials of ETX101 Gene Therapy in Dravet Syndrome at the ASGCT 2026 Presidential Symposium - BioSpace

Wed, 13 May 2026 15:39:03 GMT

Encoded Therapeutics Presents New Clinical Data from POLARIS Phase 1/2 Trials of ETX101 Gene Therapy in Dravet Syndrome at the ASGCT 2026 Presidential Symposium BioSpace

REGENXBIO Advances Duchenne Gene Therapy Toward Accelerated Approval - Benzinga

Thu, 14 May 2026 16:03:30 GMT

REGENXBIO Advances Duchenne Gene Therapy Toward Accelerated Approval Benzinga

rAAV8 HMR-001 Boosts Liver Gene Therapy in Hemophilia - Bioengineer.org

Sat, 16 May 2026 05:14:10 GMT

rAAV8 HMR-001 Boosts Liver Gene Therapy in Hemophilia Bioengineer.org

Rocket Pharmaceuticals stock (US7731221062): gene therapy hopes meet volatile trading - AD HOC NEWS

Sat, 16 May 2026 17:07:52 GMT

Rocket Pharmaceuticals stock (US7731221062): gene therapy hopes meet volatile trading AD HOC NEWS

Miracle baby treated with pioneering CRISPR gene-editing therapy at CHOP takes first steps - 6abc Philadelphia

Thu, 18 Dec 2025 08:00:00 GMT

Miracle baby treated with pioneering CRISPR gene-editing therapy at CHOP takes first steps 6abc Philadelphia

Transparency and Early Planning Are Key in Increasing Efficiency of Gene Therapy Development for Rare Diseases - National Center for Advancing Translational Sciences (.gov)

Thu, 26 Feb 2026 08:00:00 GMT

Transparency and Early Planning Are Key in Increasing Efficiency of Gene Therapy Development for Rare Diseases National Center for Advancing Translational Sciences (.gov)

Gene Therapy to Treat Profound Hearing Loss - The New England Journal of Medicine

Wed, 11 Mar 2026 07:00:00 GMT

Gene Therapy to Treat Profound Hearing Loss The New England Journal of Medicine

The FDA Approves the First-Ever Gene Therapy for Deafness, Which Aims to Restore Hearing in Kids With a Rare Inherited Condition - Smithsonian Magazine

Wed, 29 Apr 2026 07:00:00 GMT

The FDA Approves the First-Ever Gene Therapy for Deafness, Which Aims to Restore Hearing in Kids With a Rare Inherited Condition Smithsonian Magazine

Louisiana’s 1st sickle cell gene therapy patient heads home after historic treatment - WWLTV.com

Tue, 21 Apr 2026 07:00:00 GMT

Louisiana’s 1st sickle cell gene therapy patient heads home after historic treatment WWLTV.com

Medical Miracles at Penn Medicine: Breakthrough with Customized CRISPR Treatment for Patient with CPS1 - University of Pennsylvania Almanac

Tue, 16 Dec 2025 08:00:00 GMT

Medical Miracles at Penn Medicine: Breakthrough with Customized CRISPR Treatment for Patient with CPS1 University of Pennsylvania Almanac

Cystic fibrosis: new study identifies gene therapy - healthcare-in-europe.com

Thu, 30 Apr 2026 07:00:00 GMT

Cystic fibrosis: new study identifies gene therapy healthcare-in-europe.com

Vertex, CRISPR Set Lofty Goal for Casgevy Gene Therapy as Patient Starts Ramp - BioSpace

Fri, 13 Feb 2026 08:00:00 GMT

Vertex, CRISPR Set Lofty Goal for Casgevy Gene Therapy as Patient Starts Ramp BioSpace

How durable is gene therapy for haemophilia B? - Nature

Fri, 19 Sep 2025 23:13:59 GMT

How durable is gene therapy for haemophilia B? Nature

Gene therapy ‘switch’ may offer non-addictive pain relief - Penn Today

Mon, 12 Jan 2026 08:00:00 GMT

Gene therapy ‘switch’ may offer non-addictive pain relief Penn Today

Novel In Utero Gene Therapy Holds Promise for Patients with Spinal Muscular Atrophy - Johns Hopkins Medicine

Tue, 09 Sep 2025 07:00:00 GMT

Novel In Utero Gene Therapy Holds Promise for Patients with Spinal Muscular Atrophy Johns Hopkins Medicine

DNA barcoding reveals which gene-therapy nanoparticles reach targets in vivo - Phys.org

Wed, 11 Mar 2026 07:00:00 GMT

DNA barcoding reveals which gene-therapy nanoparticles reach targets in vivo Phys.org

Gene therapy platform for lysosomal storage diseases - Ricerca Malattie Genetiche Rare

Thu, 05 Feb 2026 08:00:00 GMT

Gene therapy platform for lysosomal storage diseases Ricerca Malattie Genetiche Rare