Precision Medicine

Gene Therapy for Lipid Management: Dawn of a New Era - Cureus

Sun, 12 Jul 2026 05:46:48 GMT

Gene Therapy for Lipid Management: Dawn of a New Era Cureus

Looking Beyond Gene Therapy for Treating Charcot-Marie-Tooth Disease: Carla Taveggia, PhD - NeurologyLive

Sun, 12 Jul 2026 02:15:44 GMT

Looking Beyond Gene Therapy for Treating Charcot-Marie-Tooth Disease: Carla Taveggia, PhD NeurologyLive

ARPA-H launches $160 million effort to develop custom gene editing drugs - STAT

Thu, 09 Jul 2026 15:01:54 GMT

ARPA-H launches $160 million effort to develop custom gene editing drugs STAT

FDA Expands Use of First Sickle Cell Disease Gene Therapy for Children as Young as 2 Years - Ophthalmology Advisor

Thu, 09 Jul 2026 04:00:00 GMT

FDA Expands Use of First Sickle Cell Disease Gene Therapy for Children as Young as 2 Years Ophthalmology Advisor

Gene Therapy Casgevy Approved for Younger SCD and TDT Patients - Hematology Advisor

Thu, 09 Jul 2026 04:00:00 GMT

Gene Therapy Casgevy Approved for Younger SCD and TDT Patients Hematology Advisor

HOPE-B Gene Therapy Holds Near-Normal Factor IX at Five Years - Docwire News

Sat, 11 Jul 2026 08:01:03 GMT

HOPE-B Gene Therapy Holds Near-Normal Factor IX at Five Years Docwire News

Virginia budget expands Medicaid access to sickle cell gene therapy - Virginia Mercury

Thu, 09 Jul 2026 09:26:46 GMT

Virginia budget expands Medicaid access to sickle cell gene therapy Virginia Mercury

FMR1 gene therapy restores translationally relevant phenotypes in a mouse model for fragile X syndrome - Nature

Fri, 10 Jul 2026 17:26:43 GMT

FMR1 gene therapy restores translationally relevant phenotypes in a mouse model for fragile X syndrome Nature

How a CRISPR Gene Therapy Could Change Life for Young Children With Sickle Cell Disease - Discover Magazine

Wed, 08 Jul 2026 20:35:01 GMT

How a CRISPR Gene Therapy Could Change Life for Young Children With Sickle Cell Disease Discover Magazine

Apertura Gene Therapy Announces Cooperative Research and Development Agreement with Institutes of the NIH to Test Investigational Gene Therapy for Niemann-Pick Disease Type C1 - PR Newswire

Thu, 09 Jul 2026 12:00:00 GMT

Apertura Gene Therapy Announces Cooperative Research and Development Agreement with Institutes of the NIH to Test Investigational Gene Therapy for Niemann-Pick Disease Type C1 PR Newswire

Weill Cornell Medicine Awarded Grant for Alzheimer’s Gene Therapy Research - Newsroom | Weill Cornell Medicine

Wed, 08 Jul 2026 14:07:10 GMT

Weill Cornell Medicine Awarded Grant for Alzheimer’s Gene Therapy Research Newsroom | Weill Cornell Medicine

New genetic switch could improve gene therapy for drug-resistant epilepsy - Medical Xpress

Thu, 09 Jul 2026 22:40:02 GMT

New genetic switch could improve gene therapy for drug-resistant epilepsy Medical Xpress

Feds award $43 million to Philly gene therapy research to advance treatments for rare diseases - Inquirer.com

Fri, 10 Jul 2026 15:39:20 GMT

Feds award $43 million to Philly gene therapy research to advance treatments for rare diseases Inquirer.com

Prime wins patent fight with Beam to continue work on AATD gene editing therapy - Fierce Biotech

Wed, 08 Jul 2026 15:07:01 GMT

Prime wins patent fight with Beam to continue work on AATD gene editing therapy Fierce Biotech

Gene therapy for children with sickle cell disease approved by FDA - The Hill

Wed, 08 Jul 2026 14:31:00 GMT

Gene therapy for children with sickle cell disease approved by FDA The Hill

Boy’s brain tumor tied to gene therapy - Science | AAAS

Wed, 13 May 2026 07:00:00 GMT

Boy’s brain tumor tied to gene therapy Science | AAAS

FDA Expands Casgevy Label to Children as Young as 2, Broadening Access to First CRISPR Gene Therapy for Sickle Cell Disease - BioPharm International

Mon, 06 Jul 2026 18:53:01 GMT

FDA Expands Casgevy Label to Children as Young as 2, Broadening Access to First CRISPR Gene Therapy for Sickle Cell Disease BioPharm International

Roche ends Huntington’s gene-silencing programs - STAT

Fri, 10 Jul 2026 13:37:14 GMT

Roche ends Huntington’s gene-silencing programs STAT

A second chance for gene therapy to restore natural hearing - Nature

Thu, 09 Jul 2026 09:23:33 GMT

A second chance for gene therapy to restore natural hearing Nature

The quest to save Grace — and clear the way for rare disease patients everywhere - STAT

Thu, 09 Jul 2026 08:31:50 GMT

The quest to save Grace — and clear the way for rare disease patients everywhere STAT

Vetting medical breakthroughs: What baby KJ’s CRISPR therapy teaches reporters - Association of Health Care Journalists

Wed, 08 Jul 2026 17:19:40 GMT

Vetting medical breakthroughs: What baby KJ’s CRISPR therapy teaches reporters Association of Health Care Journalists

Gene therapy cures metro New Orleans man of sickle cell, clears path for dream of becoming pilot - Verite News

Tue, 23 Jun 2026 07:00:00 GMT

Gene therapy cures metro New Orleans man of sickle cell, clears path for dream of becoming pilot Verite News

First-in-the-world gene therapy delivers missing gene directly to infant’s brain, marking historic milestone in precision medicine - News-Medical

Thu, 11 Jun 2026 07:00:00 GMT

First-in-the-world gene therapy delivers missing gene directly to infant’s brain, marking historic milestone in precision medicine News-Medical

Gene therapy reverses Fragile X deficits in mice - University of California, Riverside

Thu, 18 Jun 2026 07:00:00 GMT

Gene therapy reverses Fragile X deficits in mice University of California, Riverside

Cell, gene therapies test employers’ cost-containment strategies - Modern Healthcare News

Wed, 08 Jul 2026 10:00:00 GMT

Cell, gene therapies test employers’ cost-containment strategies Modern Healthcare News

FDA approves gene therapy for sickle cell disease in children as young as 2 years old - News Channel 5 Nashville

Fri, 10 Jul 2026 04:19:38 GMT

FDA approves gene therapy for sickle cell disease in children as young as 2 years old News Channel 5 Nashville

Integration May Be the Missing Link in Cell and Gene Therapy Development - Technology Networks

Fri, 10 Jul 2026 08:53:41 GMT

Integration May Be the Missing Link in Cell and Gene Therapy Development Technology Networks

Gene therapy for hearing loss: Tag-teaming from the lab to the clinic - Boston Children's Answers

Thu, 23 Apr 2026 07:00:00 GMT

Gene therapy for hearing loss: Tag-teaming from the lab to the clinic Boston Children's Answers

Dual-target gene therapy in Parkinson’s disease: a multicenter phase 1 trial - Nature

Wed, 10 Jun 2026 07:00:00 GMT

Dual-target gene therapy in Parkinson’s disease: a multicenter phase 1 trial Nature

Clinical response to systemic AAV gene therapy in a large animal model of late-stage lysosomal storage disease - Nature

Mon, 04 May 2026 07:00:00 GMT

Clinical response to systemic AAV gene therapy in a large animal model of late-stage lysosomal storage disease Nature

Confluence Genetics Launches Cas-CLEAR , a New CRISPR Technology Platform for Cancer Therapy - Business Wire

Thu, 09 Jul 2026 12:00:00 GMT

Confluence Genetics Launches Cas-CLEAR , a New CRISPR Technology Platform for Cancer Therapy Business Wire

US FDA approves Vertex's gene therapy for sickle cell disease in children as young as two - Reuters

Thu, 02 Jul 2026 07:00:00 GMT

US FDA approves Vertex's gene therapy for sickle cell disease in children as young as two Reuters

Roche's $575M Gene Therapy Innovation Center nears completion - The Business Journals

Wed, 08 Jul 2026 18:53:00 GMT

Roche's $575M Gene Therapy Innovation Center nears completion The Business Journals

Opus Genetics reaches FDA alignment on phase 3 registrational design for OPGx-LCA5 gene therapy - Ophthalmology Times Europe

Wed, 08 Jul 2026 10:16:43 GMT

Opus Genetics reaches FDA alignment on phase 3 registrational design for OPGx-LCA5 gene therapy Ophthalmology Times Europe

Penn, CHOP team awarded Breakthrough Prize for blindness gene therapy - Penn Medicine

Sat, 18 Apr 2026 07:00:00 GMT

Penn, CHOP team awarded Breakthrough Prize for blindness gene therapy Penn Medicine

Ocugen Eyes 3 Retinal Gene Therapy Filings as Late-Stage Pipeline Advances - Yahoo Finance

Sat, 11 Jul 2026 00:02:00 GMT

Ocugen Eyes 3 Retinal Gene Therapy Filings as Late-Stage Pipeline Advances Yahoo Finance

FDA reverses course on Regenxbio’s childhood gene therapy after rejection - STAT

Mon, 22 Jun 2026 07:00:00 GMT

FDA reverses course on Regenxbio’s childhood gene therapy after rejection STAT

Genespire and SR-Tiget show durable preclinical efficacy of liver-directed gene therapy for methylmalonic acidemia - Ricerca Malattie Genetiche Rare

Wed, 08 Jul 2026 09:29:59 GMT

Genespire and SR-Tiget show durable preclinical efficacy of liver-directed gene therapy for methylmalonic acidemia Ricerca Malattie Genetiche Rare

Did a boy’s life-saving gene therapy cause his brain tumour? - Nature

Thu, 21 May 2026 07:00:00 GMT

Did a boy’s life-saving gene therapy cause his brain tumour? Nature

Historic FDA approval brings first gene therapy for genetic deafness - Nature

Tue, 28 Apr 2026 07:00:00 GMT

Historic FDA approval brings first gene therapy for genetic deafness Nature

FDA Clears IND for Gene Therapy Candidate to Treat Rare Metabolic Disorder - National Center for Advancing Translational Sciences (.gov)

Thu, 21 May 2026 07:00:00 GMT

FDA Clears IND for Gene Therapy Candidate to Treat Rare Metabolic Disorder National Center for Advancing Translational Sciences (.gov)

Regeneron to provide gene therapy for genetic hearing loss for free - BioXconomy

Thu, 09 Jul 2026 11:00:22 GMT

Regeneron to provide gene therapy for genetic hearing loss for free BioXconomy

New Discovery Uses Salt to Overcome Major Obstacle in Gene Therapy - University of Houston

Tue, 16 Jun 2026 07:00:00 GMT

New Discovery Uses Salt to Overcome Major Obstacle in Gene Therapy University of Houston

Cleveland Clinic First-In-Human Trial of CRISPR Gene-Editing Therapy Shown to Safely Lower Cholesterol and Triglycerides - Cleveland Clinic Newsroom

Sat, 08 Nov 2025 08:00:00 GMT

Cleveland Clinic First-In-Human Trial of CRISPR Gene-Editing Therapy Shown to Safely Lower Cholesterol and Triglycerides Cleveland Clinic Newsroom

UniQure to seek FDA approval for Huntington's disease gene therapy after previous clash with agency - CNBC

Wed, 17 Jun 2026 07:00:00 GMT

UniQure to seek FDA approval for Huntington's disease gene therapy after previous clash with agency CNBC

FDA’s cell and gene therapy head steps down after 1 year - BioSpace

Tue, 30 Jun 2026 07:00:00 GMT

FDA’s cell and gene therapy head steps down after 1 year BioSpace

Gene therapy for a rare type of deafness shows lasting results - NPR

Wed, 22 Apr 2026 07:00:00 GMT

Gene therapy for a rare type of deafness shows lasting results NPR

UMass Chan licenses gene therapy for maple syrup urine disease to Plowshare Therapies - UMass Chan Medical School

Mon, 27 Apr 2026 07:00:00 GMT

UMass Chan licenses gene therapy for maple syrup urine disease to Plowshare Therapies UMass Chan Medical School

Bio-Rad Releases New Quality Control Kits for Cell and Gene Therapy - Clinical Lab Products

Tue, 07 Jul 2026 19:12:50 GMT

Bio-Rad Releases New Quality Control Kits for Cell and Gene Therapy Clinical Lab Products

Top 10 Best-Selling Gene Therapies - Genetic Engineering and Biotechnology News

Fri, 01 May 2026 07:00:00 GMT

Top 10 Best-Selling Gene Therapies Genetic Engineering and Biotechnology News

Inside UCB’s new gene therapy facility - UCB

Fri, 24 Apr 2026 13:38:03 GMT

Inside UCB’s new gene therapy facility UCB

Cell and Gene Therapy Market Size, Share | Growth Report 2034 - Fortune Business Insights

Mon, 22 Jun 2026 07:00:00 GMT

Cell and Gene Therapy Market Size, Share | Growth Report 2034 Fortune Business Insights

CRISPR gene editing of angiopoietin-like 3: toward one-time precision therapy for dyslipidaemia - Nature

Wed, 04 Mar 2026 08:00:00 GMT

CRISPR gene editing of angiopoietin-like 3: toward one-time precision therapy for dyslipidaemia Nature

Cell & Gene Therapy World Asia - Marken.

Tue, 30 Jun 2026 07:00:00 GMT

Cell & Gene Therapy World Asia Marken.

In another reversal for rare disease field, FDA to reconsider Regenxbio gene therapy - Fierce Biotech

Mon, 22 Jun 2026 07:00:00 GMT

In another reversal for rare disease field, FDA to reconsider Regenxbio gene therapy Fierce Biotech

Fractyl Health’s GLP-1 gene therapy trial given green light - Clinical Trials Arena

Mon, 11 May 2026 07:00:00 GMT

Fractyl Health’s GLP-1 gene therapy trial given green light Clinical Trials Arena

Researchers Behind World’s First Patient-Tailored CRISPR Gene Editing Therapy Named to TIME100 List of the 100 Most Influential People in the World - Children's Hospital of Philadelphia

Wed, 15 Apr 2026 07:00:00 GMT

Researchers Behind World’s First Patient-Tailored CRISPR Gene Editing Therapy Named to TIME100 List of the 100 Most Influential People in the World Children's Hospital of Philadelphia

First patient dosed in clinical trial for gene therapy FT-001 for treatment of Leber Congenital Amaurosis-2 - Ophthalmology Times Europe

Mon, 06 Jul 2026 10:00:00 GMT

First patient dosed in clinical trial for gene therapy FT-001 for treatment of Leber Congenital Amaurosis-2 Ophthalmology Times Europe

AAV9 Gene Therapy in Type II GM1 Gangliosidosis — A Phase 1–2 Trial - The New England Journal of Medicine

Fri, 06 Feb 2026 08:00:00 GMT

AAV9 Gene Therapy in Type II GM1 Gangliosidosis — A Phase 1–2 Trial The New England Journal of Medicine

FDA approves gene therapy for children with sickle cell disease ages 2+ - Yahoo

Thu, 09 Jul 2026 00:09:00 GMT

FDA approves gene therapy for children with sickle cell disease ages 2+ Yahoo

REGENXBIO bets on FDA flexibility with filing plans for Duchenne gene therapy - BioSpace

Wed, 24 Jun 2026 07:00:00 GMT

REGENXBIO bets on FDA flexibility with filing plans for Duchenne gene therapy BioSpace

Gene Editing at Scale: ARPA-H Awards $160M to Mass-Produce Rare Disease Cures - Tech Times

Fri, 10 Jul 2026 20:56:16 GMT

Gene Editing at Scale: ARPA-H Awards $160M to Mass-Produce Rare Disease Cures Tech Times

Patients win 1st damages ruling against Kolon over Invossa gene therapy - koreabiomed.com

Fri, 10 Jul 2026 07:59:58 GMT

Patients win 1st damages ruling against Kolon over Invossa gene therapy koreabiomed.com

CRISPR-Cas12a Gene Editing of HBG1 and HBG2 Promoters to Treat Sickle Cell Disease - The New England Journal of Medicine

Wed, 01 Apr 2026 21:10:56 GMT

CRISPR-Cas12a Gene Editing of HBG1 and HBG2 Promoters to Treat Sickle Cell Disease The New England Journal of Medicine

Gene therapy ‘switch’ may offer non-addictive pain relief - Penn Medicine

Wed, 07 Jan 2026 08:00:00 GMT

Gene therapy ‘switch’ may offer non-addictive pain relief Penn Medicine

Assessing DNA impurity integrity in rAAV gene therapy manufacturing - Drug Discovery News

Tue, 24 Mar 2026 17:18:33 GMT

Assessing DNA impurity integrity in rAAV gene therapy manufacturing Drug Discovery News

Greenland Mines receives Australian patent for Klotho gene therapy - Investing.com

Fri, 10 Jul 2026 13:02:26 GMT

Greenland Mines receives Australian patent for Klotho gene therapy Investing.com

UniQure plans Q3 submission for Huntington’s gene therapy after FDA reverses course—again - BioSpace

Wed, 17 Jun 2026 07:00:00 GMT

UniQure plans Q3 submission for Huntington’s gene therapy after FDA reverses course—again BioSpace

Greenland Mines (GRML) Secures Australian Patent for Klotho Gene Therapy Platform - NewMediaWire

Fri, 10 Jul 2026 19:05:30 GMT

Greenland Mines (GRML) Secures Australian Patent for Klotho Gene Therapy Platform NewMediaWire

Why Cell and Gene Therapy's Biggest Barrier Isn't Scientific - Journal of Managed Care

Fri, 01 May 2026 07:00:00 GMT

Why Cell and Gene Therapy's Biggest Barrier Isn't Scientific Journal of Managed Care

DNA shape explains crucial gene-therapy challenges - Phys.org

Thu, 26 Mar 2026 07:00:00 GMT

DNA shape explains crucial gene-therapy challenges Phys.org

Hematopoietic Stem-Cell Gene Therapy for Cystinosis - The New England Journal of Medicine

Wed, 18 Feb 2026 08:00:00 GMT

Hematopoietic Stem-Cell Gene Therapy for Cystinosis The New England Journal of Medicine

FDA Grants RMAT Designation to Inhalable Gene Therapy for Advanced Lung Tumors - Targeted Oncology

Wed, 11 Feb 2026 08:00:00 GMT

FDA Grants RMAT Designation to Inhalable Gene Therapy for Advanced Lung Tumors Targeted Oncology

Gene Therapy Shows Promise for Life-Threatening Inherited Heart Disease - Newsroom | Weill Cornell Medicine

Wed, 17 Jun 2026 07:00:00 GMT

Gene Therapy Shows Promise for Life-Threatening Inherited Heart Disease Newsroom | Weill Cornell Medicine

First-in-the-world gene therapy delivers missing gene directly to infant's brain, marking historic milestone in precision medicine - EurekAlert!

Mon, 08 Jun 2026 07:00:00 GMT

First-in-the-world gene therapy delivers missing gene directly to infant's brain, marking historic milestone in precision medicine EurekAlert!

OTP Town Hall — October 2025 Town Hall - fda.gov

Wed, 31 Dec 2025 08:00:00 GMT

OTP Town Hall — October 2025 Town Hall fda.gov

AI-powered CRISPR could lead to faster gene therapies, Stanford Medicine study finds - Stanford Medicine

Tue, 16 Sep 2025 07:00:00 GMT

AI-powered CRISPR could lead to faster gene therapies, Stanford Medicine study finds Stanford Medicine

First-in-human trial of CRISPR gene-editing therapy safely lowered cholesterol, triglycerides - www.heart.org

Sat, 08 Nov 2025 08:00:00 GMT

First-in-human trial of CRISPR gene-editing therapy safely lowered cholesterol, triglycerides www.heart.org

Regulation of sodium/calcium homeostasis by BacNav gene therapy rescues cardiac dysfunction in chronic heart failure - Science | AAAS

Fri, 20 Mar 2026 07:00:00 GMT

Regulation of sodium/calcium homeostasis by BacNav gene therapy rescues cardiac dysfunction in chronic heart failure Science | AAAS

Experimental Gene Therapy Shields Brain from Toxic Protein Damage - UC San Diego Today

Tue, 26 May 2026 07:00:00 GMT

Experimental Gene Therapy Shields Brain from Toxic Protein Damage UC San Diego Today

Gene therapy for cardiac and vascular disease - Nature

Thu, 09 Apr 2026 13:27:01 GMT

Gene therapy for cardiac and vascular disease Nature

Single-Dose Gene Therapy Shows Promising Safety, Efficacy, and Patient-Reported Outcomes in Hemophilia B - Docwire News

Wed, 11 Mar 2026 07:00:00 GMT

Single-Dose Gene Therapy Shows Promising Safety, Efficacy, and Patient-Reported Outcomes in Hemophilia B Docwire News

FDA puts REGENXBIO gene therapy trials on hold after brain tumour - Clinical Trials Arena

Wed, 28 Jan 2026 08:00:00 GMT

FDA puts REGENXBIO gene therapy trials on hold after brain tumour Clinical Trials Arena

Cystic fibrosis: new study identifies gene therapy - healthcare-in-europe.com

Thu, 30 Apr 2026 07:00:00 GMT

Cystic fibrosis: new study identifies gene therapy healthcare-in-europe.com

Transparency and Early Planning Are Key in Increasing Efficiency of Gene Therapy Development for Rare Diseases - National Center for Advancing Translational Sciences (.gov)

Thu, 26 Feb 2026 08:00:00 GMT

Transparency and Early Planning Are Key in Increasing Efficiency of Gene Therapy Development for Rare Diseases National Center for Advancing Translational Sciences (.gov)

New Australian patent backs Klotho gene therapy targeting ALS and other neuromuscular diseases - Stock Titan

Fri, 10 Jul 2026 12:00:00 GMT

New Australian patent backs Klotho gene therapy targeting ALS and other neuromuscular diseases Stock Titan

Cliona Rooney and Bambi Grilley Are Advancing Cell and Gene Therapy Through Leadership and Mentorship - Texas Children’s

Wed, 01 Jul 2026 22:45:57 GMT

Cliona Rooney and Bambi Grilley Are Advancing Cell and Gene Therapy Through Leadership and Mentorship Texas Children’s

Jaguar Gene Therapy completes Cohort I patient dosing in JAG201 trial - Clinical Trials Arena

Wed, 25 Feb 2026 08:00:00 GMT

Jaguar Gene Therapy completes Cohort I patient dosing in JAG201 trial Clinical Trials Arena

Man functionally cured of sickle cell disease through gene therapy - WISN

Sun, 05 Jul 2026 14:29:00 GMT

Man functionally cured of sickle cell disease through gene therapy WISN

Phase 1 Trial of CRISPR-Cas9 Gene Editing Targeting ANGPTL3 - The New England Journal of Medicine

Sat, 08 Nov 2025 08:00:00 GMT

Phase 1 Trial of CRISPR-Cas9 Gene Editing Targeting ANGPTL3 The New England Journal of Medicine

FDA fully releases clinical hold on Intellia CRISPR gene therapy trials - Fierce Biotech

Mon, 02 Mar 2026 08:00:00 GMT

FDA fully releases clinical hold on Intellia CRISPR gene therapy trials Fierce Biotech

First Gene Regulation Clinical Trials for Epilepsy Show Promising Results - Northwestern University

Wed, 11 Mar 2026 07:00:00 GMT

First Gene Regulation Clinical Trials for Epilepsy Show Promising Results Northwestern University

Shooting for the stars: UVA lab’s new gene therapy may end pediatric seizures - UVA Today

Wed, 24 Jun 2026 14:54:10 GMT

Shooting for the stars: UVA lab’s new gene therapy may end pediatric seizures UVA Today

Intracerebroventricular SPAST-AAV9 gene therapy prevents manifestation of symptoms in a mouse model of SPG4 hereditary spastic paraplegia - ScienceDirect.com

Wed, 04 Mar 2026 08:00:00 GMT

Intracerebroventricular SPAST-AAV9 gene therapy prevents manifestation of symptoms in a mouse model of SPG4 hereditary spastic paraplegia ScienceDirect.com

Opus aligns with FDA on rare eye disease gene therapy trial - BioWorld News

Tue, 07 Jul 2026 16:00:00 GMT

Opus aligns with FDA on rare eye disease gene therapy trial BioWorld News

Lilly stops development of three drugs, including gene therapy - Clinical Trials Arena

Thu, 05 Feb 2026 08:00:00 GMT

Lilly stops development of three drugs, including gene therapy Clinical Trials Arena

Roche ends 2 Huntington’s disease programs, including Ionis-partnered tominersen - Fierce Biotech

Thu, 09 Jul 2026 18:40:16 GMT

Roche ends 2 Huntington’s disease programs, including Ionis-partnered tominersen Fierce Biotech

Gene Therapy to Treat Profound Hearing Loss - The New England Journal of Medicine

Wed, 11 Mar 2026 07:00:00 GMT

Gene Therapy to Treat Profound Hearing Loss The New England Journal of Medicine

Potential gene therapy for late-stage Parkinson's side-effects uncovered - Medical Xpress

Wed, 03 Jun 2026 07:00:00 GMT

Potential gene therapy for late-stage Parkinson's side-effects uncovered Medical Xpress

$2 Million Gene Therapy Cures Require a Financing Model - USC Schaeffer

Mon, 15 Jun 2026 07:00:00 GMT

$2 Million Gene Therapy Cures Require a Financing Model USC Schaeffer